Noninvasive gene transfer to the lung for systemic delivery of therapeutic proteins. (Q34777289)

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12189244%20AND%20SRC:MED&resulttype=core&format=json

12 November 2019

title

Noninvasive gene transfer to the lung for systemic delivery of therapeutic proteins (English)

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12 November 2019

3

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12 November 2019

James Wilson

8

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12 November 2019

1

Alberto Auricchio

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12 November 2019

author name string

Erin O'Connor

2

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12 November 2019

Guang-Ping Gao

4

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12 November 2019

Markus Hildinger

5

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12 November 2019

Lili Wang

6

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12 November 2019

Roberto Calcedo

7

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12 November 2019

language of work or name

English

0 references

publication date

1 August 2002

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Journal of Clinical Investigation

12 November 2019

published in

1 reference

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12 November 2019

volume

110

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12 November 2019

issue

4

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12 November 2019

page(s)

499-504

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The lung as a route for systemic delivery of therapeutic proteins and peptides

12 November 2019

cites work

1 reference

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Gene therapy for hemophilia B: AAV-mediated transfer of the gene for coagulation factor IX to human muscle.

7 July 2018

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Adeno-associated virus type 6 (AAV6) vectors mediate efficient transduction of airway epithelial cells in mouse lungs compared to that of AAV2 vectors

7 July 2018

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Hybrid vectors based on adeno-associated virus serotypes 2 and 5 for muscle-directed gene transfer

7 July 2018

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Binding of adeno-associated virus type 5 to 2,3-linked sialic acid is required for gene transfer

7 July 2018

1 reference

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Filovirus-pseudotyped lentiviral vector can efficiently and stably transduce airway epithelia in vivo

7 July 2018

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Isolation of highly infectious and pure adeno-associated virus type 2 vectors with a single-step gravity-flow column.

7 July 2018

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Gene transfer as an approach to treating hemophilia

7 July 2018

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Adeno-associated virus vectors for gene therapy: more pros than cons?

7 July 2018

1 reference

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Purification of recombinant adeno-associated virus vectors by column chromatography and its performance in vivo

7 July 2018

1 reference

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Sustained expression of therapeutic level of factor IX in hemophilia B dogs by AAV-mediated gene therapy in liver

7 July 2018

1 reference

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Endosomal processing limits gene transfer to polarized airway epithelia by adeno-associated virus.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Adeno-associated virus type 5 (AAV5) but not AAV2 binds to the apical surfaces of airway epithelia and facilitates gene transfer

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Evidence for gene transfer and expression of factor IX in haemophilia B patients treated with an AAV vector.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Repeat transduction in the mouse lung by using adeno-associated virus vectors with different serotypes

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Persistent expression of canine factor IX in hemophilia B canines

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Transduction of well-differentiated airway epithelium by recombinant adeno-associated virus is limited by vector entry.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Gene therapy vectors based on adeno-associated virus type 1.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Sustained correction of bleeding disorder in hemophilia B mice by gene therapy

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Cloning and characterization of adeno-associated virus type 5.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Successful readministration of adeno-associated virus vectors to the mouse lung requires transient immunosuppression during the initial exposure

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Factors influencing recombinant adeno-associated virus production

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

A factor IX-deficient mouse model for hemophilia B gene therapy

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Cloning of adeno-associated virus type 4 (AAV4) and generation of recombinant AAV4 particles.

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Haemophilia prophylaxis in young patients--a long-term follow-up

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Stable gene transfer and expression of human blood coagulation factor IX after intramuscular injection of recombinant adeno-associated virus

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Transduction with recombinant adeno-associated virus for gene therapy is limited by leading-strand synthesis

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Stable in vivo expression of the cystic fibrosis transmembrane conductance regulator with an adeno-associated virus vector

7 July 2018

1 reference

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Cloning of adeno-associated virus into pBR322: rescue of intact virus from the recombinant plasmid in human cells

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Phenotypic correction of factor IX deficiency in skin fibroblasts of hemophilic dogs

7 July 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Adenovirus-mediated transfer of a recombinant alpha 1-antitrypsin gene to the lung epithelium in vivo

7 July 2018

1 reference

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cis-acting elements that confer lung epithelial cell expression of the CC10 gene

7 July 2018

1 reference

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Muscle-directed gene transfer and transient immune suppression result in sustained partial correction of canine hemophilia B caused by a null mutation

7 July 2018

1 reference

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Several log increase in therapeutic transgene delivery by distinct adeno-associated viral serotype vectors

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Direct intramuscular injection with recombinant AAV vectors results in sustained expression in a dog model of hemophilia

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Gene therapy for the hemophilias

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Recombinant adeno-associated virus for muscle directed gene therapy

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

Molecular cloning of adeno-associated virus variant genomes and generation of infectious virus by recombination in mammalian cells

26 October 2018

1 reference

https://eutils.ncbi.nlm.nih.gov/entrez/eutils/elink.fcgi?dbfrom=pmc&linkname=pmc_refs_pubmed&retmode=json&id=150421

26 October 2018

Identifiers

DOI

10.1172/JCI0215780

1 reference

PubMed publication ID

4 August 2017

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12189244%20AND%20SRC:MED&resulttype=core&format=json

12 November 2019

1 reference

https://www.ebi.ac.uk/europepmc/webservices/rest/search?query=EXT_ID:12189244%20AND%20SRC:MED&resulttype=core&format=json

12 November 2019

PubMed publication ID

12189244

1 reference