Viral vectors for gene transfer of micro-, mini-, or full-length dystrophin (Q34807084)

4 August 2017

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title

Viral vectors for gene transfer of micro-, mini-, or full-length dystrophin (English)

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4 August 2017

Jeannine M Scott

1

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4 August 2017

Sheng Li

2

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4 August 2017

Scott Q Harper

3

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4 August 2017

Robert Welikson

4

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4 August 2017

Daniel Bourque

5

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4 August 2017

Christiana DelloRusso

6

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4 August 2017

Stephen D Hauschka

7

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4 August 2017

Jeffrey S Chamberlain

8

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4 August 2017

publication date

1 October 2002

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4 August 2017

published in

Neuromuscular Disorders

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4 August 2017

volume

12 Suppl 1

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4 August 2017

page(s)

S23-9

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Complete cloning of the duchenne muscular dystrophy (DMD) cDNA and preliminary genomic organization of the DMD gene in normal and affected individuals

4 August 2017

cites work

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Dystrophin: the protein product of the Duchenne muscular dystrophy locus

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7 January 2021

Encapsidated adenovirus minichromosomes allow delivery and expression of a 14 kb dystrophin cDNA to muscle cells

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7 January 2021

A new adenoviral vector: Replacement of all viral coding sequences with 28 kb of DNA independently expressing both full-length dystrophin and beta-galactosidase

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7 January 2021

Generation and growth of gutted adenoviral vectors

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7 January 2021

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7 January 2021

Efficient long-term gene transfer into muscle tissue of immunocompetent mice by adeno-associated virus vector

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7 January 2021

Efficient and stable adeno-associated virus-mediated transduction in the skeletal muscle of adult immunocompetent mice

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7 January 2021

Recombinant adeno-associated virus for muscle directed gene therapy

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7 January 2021

The complete sequence of dystrophin predicts a rod-shaped cytoskeletal protein

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7 January 2021

Is the carboxyl-terminus of dystrophin required for membrane association? A novel, severe case of duchenne muscular dystrophy

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7 January 2021

Half the dystrophin gene is apparently enough for a mild clinical course: confirmation of its potential use for gene therapy.

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7 January 2021

Very mild muscular dystrophy associated with the deletion of 46% of dystrophin

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7 January 2021

Overexpression of dystrophin in transgenic mdx mice eliminates dystrophic symptoms without toxicity

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7 January 2021

Expression of full-length and truncated dystrophin mini-genes in transgenic mdx mice

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7 January 2021

Transgenic mdx mice expressing dystrophin with a deletion in the actin-binding domain display a "mild Becker" phenotype

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7 January 2021

Expression of Dp260 in muscle tethers the actin cytoskeleton to the dystrophin-glycoprotein complex and partially prevents dystrophy.

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7 January 2021

Assembly of the dystrophin-associated protein complex does not require the dystrophin COOH-terminal domain

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7 January 2021

Forced expression of dystrophin deletion constructs reveals structure-function correlations.

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7 January 2021

Modular flexibility of dystrophin: implications for gene therapy of Duchenne muscular dystrophy

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7 January 2021

Immune evasion by muscle-specific gene expression in dystrophic muscle

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7 January 2021

Analysis of muscle creatine kinase regulatory elements in recombinant adenoviral vectors

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7 January 2021

Infectious clones and vectors derived from adeno-associated virus (AAV) serotypes other than AAV type 2.

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7 January 2021

In vivo gene delivery and stable transduction of nondividing cells by a lentiviral vector

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7 January 2021

Sustained expression of genes delivered directly into liver and muscle by lentiviral vectors

1 reference

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7 January 2021

Transduction of a gene expression cassette using advanced generation lentiviral vectors

1 reference

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7 January 2021

Lentivirus Vectors Encoding Both Central Polypurine Tract and Posttranscriptional Regulatory Element Provide Enhanced Transduction and Transgene Expression

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7 January 2021

Improved adenoviral vectors for gene therapy of Duchenne muscular dystrophy

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7 January 2021

Gutted adenoviral vector growth using E1/E2b/E3-deleted helper viruses

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7 January 2021

Massive idiosyncratic exon skipping corrects the nonsense mutation in dystrophic mouse muscle and produces functional revertant fibers by clonal expansion

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7 January 2021

Suppression of revertant fibers in mdx mice by expression of a functional dystrophin.

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7 January 2021

Hematopoietic potential of stem cells isolated from murine skeletal muscle

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7 January 2021

Dystrophin expression in the mdx mouse restored by stem cell transplantation

1 reference

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7 January 2021

Growth factor control of skeletal muscle differentiation: commitment to terminal differentiation occurs in G1 phase and is repressed by fibroblast growth factor

1 reference

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7 January 2021

Characterization of dystrophin and utrophin diversity in the mouse

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7 January 2021

10.1016/S0960-8966(02)00078-0

Identifiers

DOI

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4 August 2017

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